The Margolis Rich Family

Six-year-old Lily was diagnosed with a rare gene mutation before her 2nd birthday. Committed to exploring alternative paths forward, Lily's parents Darren Margolis and Carrie Rich partnered with an innovative scientific research platform called Rarebase to explore whether there could be an FDA approved repurposed drug that might target Lily’s rare gene mutation. Rarebase leverages biology and cutting-edge artificial intelligence technology to rapidly discover and develop treatments for millions of people worldwide living with a rare disease.